Gene Therapy for SCID Provides New Hope for Two Siblings

Colton and Abbygail Ainslie

Siblings Colton and Abbygail Ainslie were among 10 U.S. children enrolled in a clinical trial at UCLA to test the use of gene therapy in treating ADA SCID. Three of the 10 children are now healthy.  Results of this 11-year study were reported in the peer-reviewed journal Blood on Tuesday, September 11, 2012. Read more about Colton and Abbygail from TODAY.com http://todayhealth.today.com/_news/2012/09/11/13804809-siblings-among-first-cured-of-bubble-boy-disease?lite